Focus Session
Organized by Berlin Institute of Health (BIH) at Charité Berlin
In this focus session, we will explore the opportunities and challenges associated with the development of stem cell-based therapies within the broader context of gene and cell-based therapies. The session will kick off with an introductory talk by Giulio Cossu, who will highlight the obstacles encountered in the translational process and the complexities of establishing a sustainable framework for delivering these therapies to patients, particularly those with rare diseases. Participants will be introduced to two distinct cases demonstrating how Advanced Therapy Medicinal Products (ATMPs) can reach patients, despite commercialization hurdles. Moreover, the session will delve into various strategies adopted across Europe to support the advancement of gene and cell therapy. We will examine the German national strategy for gene and cell therapy, the initiative by French INSERM PEPR Biotherapies and Bioproduction for innovative therapies, and the efforts of the UK Catapult for Cell and Gene Therapy. A panel discussion will provide insights into how these approaches address the promising opportunities and challenges in the field. This focus session aims to provide a comprehensive overview of the current landscape and future directions in stem cell-based therapy development, emphasizing collaborative and innovative strategies to navigate the existing hurdles.