STEM CELLS FOR PERSONALIZED MEDICINE

Sponsored By 

Concurrent Speaker(s)

• 

  Jeffrey Beekman, PhD

  -
  University Medical Center Utrecht, Netherlands
• 

  Eva van Rooij, PhD

  Hubrecht Institute, Netherlands

Presenting Author(s)

• AG

  Aman George, PhD

  Ophthalmic Genetics and Visual Function Branch
  National Institutes of Health, United States
• 

  Nathalie Saurat, PhD

  The Center for Stem Cell Biology and Developmental Biology Program
  MSKCC, USA
• 

  Tianyuan Shi, PhD (she/her/hers)

  School of Biomedical Sciences
  The University of Hong Kong, Hong Kong
• 

  Abel Vertesy, PhD

  Knoblich Lab
  IMBA - Institute of Molecular Biotechnology Austria, Austria

This session will explore how the generation of stem cell models from patients with genetic diseases has increasingly improved to the extent that they can now predict disease phenotypes and even be used for drug discovery to correct the condition.

Presentations:

• IDENTIFYING NEW MECHANISMS AND THERAPEUTIC OPPORTUNITIES FOR CARDIOMYOPATHY
  

  Concurrent Speaker: Eva van Rooij, PhD – Hubrecht Institute
• PROGRAMMING AGE IN HUMAN STEM CELL MODELS OF NEURODEGENERATIVE DISEASE
  

  Presenting Author: Nathalie Saurat, PhD – MSKCC
• GENE THERAPY INDUCES PIGMENTATION IN INDUCED PLURIPOTENT STEM CELLS DERIVED RETINAL PIGMENT EPITHELIUM FROM OCA1A PATIENTS AND ALBINO RAT EYE
  

  Presenting Author: Aman George, PhD – National Institutes of Health
• HIGH-THROUGHPUT NEURAL CONNECTIVITY MAPPING IN HUMAN BRAIN ORGANOIDS
  

  Presenting Author: Abel Vertesy, PhD – IMBA - Institute of Molecular Biotechnology Austria
• RESTORING DELETED IN LIVER CANCER 1 (DLC1) ISOFORM 1 EXPRESSION IS A MORE EFFECTIVE GENE THERAPY FOR SPINAL MUSCULAR ATROPHY
  

  Presenting Author: Tianyuan Shi, PhD (she/her/hers) – The University of Hong Kong
• INTESTINAL ORGANOIDS FOR CYSTIC FIBROSIS PRECISION MEDICINE
  

  Concurrent Speaker: Jeffrey Beekman, PhD – University Medical Center Utrecht